CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores mitochondrial homeostasis in dominant optic atrophy patient-derived iPSCs: Molecular Therapy - Nucleic Acids
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CRISPR-Cas9 correction of OPA1 c.1334G>A: p.R445H restores
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Frontiers Establishing induced pluripotent stem cell lines from
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